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orphan drug designation

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Pharmaceutical Investing

La Jolla Pharmaceutical Company Receives Orphan Designation from FDA for LJPC-0118

NASDAQ:CPRX
Pharmaceutical Investing

Catalyst Pharmaceuticals Files Lawsuit Against FDA Over Rival Drug

Applied Therapeutics Announces FDA Orphan Drug Designation for AT-007

Equillium Granted U.S. FDA Orphan Drug Designations for EQ001

NASDAQ:PRAN

Prana Granted First MSA Orphan Drug Designation from FDA

FDA Grants Cerecor’s Three Substrate Replacement Therapies Orphan Drug Designation

Apellis Pharmaceuticals’ APL-2 Receives Orphan Drug Designation from the FDA

Mustang Bio Receives Orphan Drug Designation for MB-102 (CD123 CAR T) for the Treatment of Blastic Plasmacytoid Dendritic Cell Neoplasm

Pluristem Therapeutics Announces FDA Orphan Drug Designation for PLX cell therapy

Adverum Biotechnologies Receives Orphan Drug Designation for ADVM-053, a Novel Gene Therapy Candidate for the Treatment of Hereditary Angioedema

Ironwood Pharmaceuticals Announces FDA Orphan Drug Designation for Olinciguat for the Treatment of Sickle Cell Disease

Ascendis Pharma Announces Orphan Drug Designation Granted for TransCon PTH as Treatment for Hypoparathyroidism

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