BioMarin Presents New Data on the Positive Impact of Early Treatment With VOXZOGO® on Proportionality and Arm Span in Children with Achondroplasia at the 2026 American College of Medical Genetics and Genomics Annual Clinical Genetics Meeting 12 March
U.S. Food and Drug Administration Approves BioMarin's PALYNZIQ® for Adolescents 12 Years of Age and Older with Phenylketonuria 27 February